Very sad to see such a poorly designed study. Note that many guidelines on how to do this properly are available: see e.g. this @TREAT_NMD paper https://t.co/dvbg5H3aBK which includes obvious things like including wild type references and much more.
RT @oligogirl: They suggest setting up disease specific taskforces to discuss parameters and guidelines. Agreed! This is something @TREAT_N…
RT @oligogirl: They suggest setting up disease specific taskforces to discuss parameters and guidelines. Agreed! This is something @TREAT_N…
RT @oligogirl: They suggest setting up disease specific taskforces to discuss parameters and guidelines. Agreed! This is something @TREAT_N…