You mean like for Leber's congenital amaurosis ([PNAS...
User dbissig, in the askscience subreddit,
You mean like for Leber's congenital amaurosis ([PNAS article](http://www.ncbi.nlm.nih.gov/pmc/articles/PMC2567501/?tool=pubmed)…
You mean like for Leber's congenital amaurosis ([PNAS article](http://www.ncbi.nlm.nih.gov/pmc/articles/PMC2567501/?tool=pubmed)…
>will be a practical solution [...] like cystic fibrosis and sickle…
> Induced pluripotent stem cells are even further off than embryonic stem cells for use as therapeutics. They require a high…