Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR-Cas9 gene editing
Article in Molecular Therapy — Methods & Clinical Development (October 2023)
The most recent citing publications are shown below. View all 26 publications that cite this research output on Dimensions.
Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor
Article in Molecular Therapy (March 2023)
The origin of unwanted editing byproducts in gene editing
Article in Acta Biochimica et Biophysica Sinica (May 2022)