Caregiver perspectives on patient-focused drug development for Phelan-McDermid syndrome
Article in Orphanet Journal of Rare Diseases (March 2024)
The most recent citing publications are shown below. View all 14 publications that cite this research output on Dimensions.
Article in Orphanet Journal of Rare Diseases (March 2024)
Article in Biomedicines (January 2024)
Article in Pediatric Research (September 2023)