The evolution of adeno-associated virus capsids for CNS gene therapy
BioInsights,
CNS gene therapy: how we got to where we are now The first CNS-directed AAV gene therapy trials started in the early 2000s…
CNS gene therapy: how we got to where we are now The first CNS-directed AAV gene therapy trials started in the early 2000s…
Mandel RJ, Marmion DJ, Kirik D, Chu Y, Heindel C, McCown T, Gray SJ, Kordower JH.