Randomized controlled trial data for successful new drug application for rare diseases in the United States
Article in Orphanet Journal of Rare Diseases (April 2023)
The most recent citing publications are shown below. View all 20 publications that cite this research output on Dimensions.
Article in Orphanet Journal of Rare Diseases (April 2023)
Article in Orphanet Journal of Rare Diseases (June 2022)
Article in Therapeutic Innovation & Regulatory Science (April 2022)