Investigating health-related quality of life in rare diseases: a case study in utility value determination for patients with CLN2 disease (neuronal ceroid lipofuscinosis type 2)
Article in Orphanet Journal of Rare Diseases (May 2021)
The most recent citing publications are shown below. View all 7 publications that cite this research output on Dimensions.
Article in Orphanet Journal of Rare Diseases (May 2021)
Article in MDM Policy & Practice (January 2020)
Article in PLOS ONE (March 2018)