61 followers
@dedwng https://t.co/aLKTazhyV6 has a comprehensive overview, study design and results, for AMYTs trial. Think FDA will be lenient given dearth of DEB treatments, will be interesting to see.
@dedwng https://t.co/aLKTazhyV6 has a comprehensive overview, study design and results, for AMYTs trial. Think FDA will be lenient given dearth of DEB treatments, will be interesting to see.
@dedwng From AMYT EASE trial (https://t.co/aLKTazhyV6), "the two-week confirmatory assessment was reduced to one week because of the tendency of EB wounds to re-open per the normal course of the disease state." Still, 30% placebo rsp is concerning, so not