Bibliosalut, 02 Feb 2021 #PublicaSalutIB Seguretat a llarg termini i eficàcia del patisiran per amiloidosi hereditària mitjançada per transtiretina amb…
Neurology Today, 17 Nov 2020 Patisiran seems to have an acceptable safety profile and sustained efficacy in patients with hereditary transthyretin-mediated…