METHODS AND COMPOSITIONS FOR THE TREATMENT OF CYTOPPLASMIC GLYCOGEN STORAGE DISORDERS Application EP-3344337-A4 European Patent Office 06 Mar 2019
ENZYMATIC REPLACEMENT THERAPY AND ANTISENSE THERAPY FOR POMPE DISEASE Application WO-2018231060-A1 World Intellectual Property Organisation (WIPO) 20 Dec 2018
NATURAL CRYPTIC EXON REMOVAL BY PAIRS OF ANTISENSE OLIGONUCLEOTIDES Application WO-2018026284-A1 World Intellectual Property Organisation (WIPO) 08 Feb 2018
Methods of lysosomal storage disease therapy Grant US-8679478-B2 United States of America 25 Mar 2014