Characterization of early markers of disease in the mouse model of mucopolysaccharidosis IIIB
Article in Journal of Neurodevelopmental Disorders (April 2024)
The most recent citing publications are shown below. View all 160 publications that cite this research output on Dimensions.
Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy
Article in Molecular Therapy (November 2023)
Nanomedicines to treat rare neurological disorders: The case of Krabbe disease
Article in Advanced Drug Delivery Reviews (October 2023)