Thinking about the 17-year statistic (delay between research findings and benefit to patients), especially in the rare disorder (#XLH) context. Good article but not on point for my concern about what happens AFTER FDA approval: https://t.co/Gx4Vz8ia9X
Role of Translational Science in #RareDisease Innovation, Discovery, & Drug Development. https://t.co/rndRJDGz6n More POVs & articles needed
RT @aHUSAmerica: Role of #Translational Science in #RareDisease Innovation, Discovery & Development of #orphandrugs. https://t.co/wAY05QtrP…
Role of #Translational Science in #RareDisease Innovation, Discovery & Development of #orphandrugs. https://t.co/wAY05QtrPQ #research #aHUS https://t.co/OGd5OImDg7