Successful treatment of severe MSUD in Bckdhb−/− mice with neonatal AAV gene therapy
Article in Journal of Inherited Metabolic Disease (March 2023)
The most recent citing publications are shown below. View all 13 publications that cite this research output on Dimensions.
Article in Journal of Inherited Metabolic Disease (March 2023)
Article in Metabolic Brain Disease (August 2022)
Book chapter (June 2022)