@floszcrxl I hope the scientific community learned from this $qure study which appears to have given the families and children in the study a little more time. I hope it leads to an eventual cure. Some of the knowledge gained could help w current qure tria
May,2021: Cell-Mediated Immunity to NAGLU Transgene Following Intracerebral Gene Therapy in Children With Mucopolysaccharidosis Type IIIB Syndrome https://t.co/yCC274onNo
Cc: @adamjshay
Cell-Mediated Immunity to NAGLU Transgene Following Intracerebral Gene Therapy in Children With Mucopolysaccharidosis Type IIIB Syndrome https://t.co/yCC274onNo #SanfilippoB #MPSIIIB (AMT-110 $QURE suspended this program in 2016) https://t.co/4qlM6u19Zj