Gene replacement therapy for spinal muscular atrophy: safety and preliminary efficacy in a Brazilian cohort
Article in Gene Therapy (June 2024)
The most recent citing publications are shown below. View all 46 publications that cite this research output on Dimensions.
Article in Gene Therapy (June 2024)
Book chapter (May 2024)
Article in Journal of Children's Orthopaedics (March 2024)