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RT @NatRevDrugDisc: FDA approves gene therapy for metachromatic leukodystrophy https://t.co/E0p5OSrd1W Atidarsagene autotemcel (Lenmeldy)…
RT @NatRevDrugDisc: FDA approves gene therapy for metachromatic leukodystrophy https://t.co/E0p5OSrd1W Atidarsagene autotemcel (Lenmeldy)…
Gene Therapy coming in action!!!
RT @NatRevDrugDisc: FDA approves gene therapy for metachromatic leukodystrophy https://t.co/E0p5OSrd1W Atidarsagene autotemcel (Lenmeldy)…
RT @salonium: Fascinating read about the world's newest most expensive drug ($4M) A one-off treatment for metachromatic leukodystrophy, a…