Exon skipping induces uniform dystrophin rescue with dose-dependent restoration of serum miRNA biomarkers and muscle biophysical properties
Article in Molecular Therapy - Nucleic Acids (August 2022)
The most recent citing publications are shown below. View all 24 publications that cite this research output on Dimensions.
PPMO-mediated exon skipping induces uniform sarcolemmal dystrophin rescue with dose-dependent restoration of circulating microRNA biomarkers and muscle biophysical properties
Preprint in bioRxiv (January 2022)
Circulating Biomarkers in Muscular Dystrophies: Disease and Therapy Monitoring
Article in Molecular Therapy — Methods & Clinical Development (May 2020)