Facioscapulohumeral Muscular Dystrophy European Patient Survey: Assessing Patient Reported Disease Burden and Preferences in Clinical Trial Participation
Article in Journal of Neuromuscular Diseases (March 2024)
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Article in Journal of Neuromuscular Diseases (March 2024)
Article in Health Expectations (January 2024)
Preprint in medRxiv (December 2023)