AAV-mediated delivery of secreted acid α-glucosidase with enhanced uptake corrects neuromuscular pathology in Pompe mice
Article in JCI Insight (August 2023)
The most recent citing publications are shown below. View all 46 publications that cite this research output on Dimensions.
GAA deficiency disrupts distal airway cells in Pompe disease
Article in American Journal of Physiology - Lung Cellular and Molecular Physiology (June 2023)
Chemogenetic activation of hypoglossal motoneurons in a mouse model of Pompe disease
Article in Journal of Neurophysiology (August 2022)