Combinations for the modulation of SMN expression Grant US-11198867-B2 United States of America 14 Dec 2021
Method for increasing the activity of a cystic fibrosis transmembrane conductance… Grant US-9994856-B2 United States of America 12 Jun 2018
Compositions and methods for modulation of SMN2 splicing in a subject Grant US-9926559-B2 United States of America 27 Mar 2018