Efficacy and safety of a SOD1-targeting artificial miRNA delivered by AAV9 in mice are impacted by miRNA scaffold selection
Article in Molecular Therapy - Nucleic Acids (October 2023)
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Article in Molecular Therapy - Nucleic Acids (October 2023)
Article in International Journal of Molecular Sciences (September 2023)
Article in International Journal of Molecular Sciences (January 2023)