Open‐label, single‐center, clinical study evaluating the safety, tolerability and clinical effects of pentosan polysulfate sodium in subjects with mucopolysaccharidosis I
Article in Journal of Inherited Metabolic Disease (March 2024)
The most recent citing publications are shown below. View all 28 publications that cite this research output on Dimensions.
Article in Journal of Inherited Metabolic Disease (March 2024)
Article in Cells (August 2023)
Article in Pharmaceuticals (March 2023)