Therapeutic Role of Nusinersen on Respiratory Progression in Pediatric Patients With Spinal Muscular Atrophy Type 2 and Nonambulant Type 3
Article in Neurology Clinical Practice (June 2024)
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Article in Neurology Clinical Practice (June 2024)
Preprint in Preprints.org (April 2024)
Article in Neurological Sciences (April 2024)