Preclinical Development of Antisense Oligonucleotides to Rescue Aberrant Splicing Caused by an Ultrarare ABCA4 Variant in a Child with Early-Onset Stargardt Disease
Article in Cells (March 2024)
The most recent citing publications are shown below. View all 2 publications that cite this research output on Dimensions.
Article in Cells (March 2024)
Article in Genes (January 2023)